The Voice of the Patient report is critical for researchers to submit new therapies to the FDA for regulatory approval. It will also inform the clinical trial endpoints that are important to our community.
Conference: 10th International Scientific, Medical & Family Conference
When:Jul 20, 2020. Ends on Jul 25, 2020.
Where:400 Mandalay Ave.,
One meeting brings together doctors and scientists involved in the many aspects of Barth syndrome to discuss the latest underlying scientific developments and clinical insights. The other is a family meeting in which the latest information is shared.